PANTHERx® Specialty Pharmacy Selected by Ultragenyx to Distribute Crysvita

PANTHERx® Specialty Pharmacy (PANTHERx®), THE Rare Disease Specialty Pharmacy®, announced that it has been selected by Ultragenyx Pharmaceutical, Inc. to distribute Crysvita™ (burosumab-twza), the very first FDA-approved therapy for children and adults with x-linked hypophosphatemia (XLH). PANTHERx® is one of a select few specialty pharmacies providing nationwide access to the medication.

Crysvita (burosumab-twza) is the first drug approved to treat adults and children ages one year and older with x-linked hypophosphatemia (XLH).  XLH causes low levels of phosphorus in the blood. It leads to impaired bone growth and development in children and adolescents and problems with bone mineralization throughout a patient’s life.  XLH is a serious disease affecting approximately 3,000 children and 12,000 adults in the United States. Most children with XLH experience bowed or bent legs, short stature, bone pain and severe dental pain. Some adults with XLH experience persistent discomfort or complications, such as joint pain, impaired mobility, tooth abscesses and hearing loss.

“The approval of Crysvita marks a turning point for patients and families who have waited what seems an eternity for a breakthrough treatment for XLH,” said Dr. Gordon Vanscoy, Chairman and CEO at PANTHERx®. “The therapy offers hope to patients, families, and caregivers and PANTHERx® is proud to support them.”

For more information about RareCareTM services for patients with XLH, contact us at 833-599-2245 or email

About PANTHERx® Specialty Pharmacy

PANTHERx® Specialty Pharmacy, THE Rare Disease Specialty Pharmacy®, is quad-accredited and a back-to-back Zitter Health Insights Patient Choice Award winner headquartered in Pittsburgh, Pennsylvania. PANTHERx® Specialty’s mission is to transform lives by delivering medical breakthroughs, clinical excellence, and access solutions to patients afflicted with rare and devastating conditions. PANTHERx® works daily to Reinvent Specialty, Revolutionize Pharmacy, and Redefine Care®, by developing focused solutions, bold innovations, and novel clinical services associated with life-transforming therapies.


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